Treatment Archives

NPR Spotlights Zatolmilast: A Potential Breakthrough for Fragile X Syndrome

October 1, 2024

NPR spotlights zatolmilast, a promising investigational drug to treat Fragile X syndrome. Families report life-changing improvements in learning and independence.

NPR Feature – A Fragile X Treatment May Be On The Horizon

May 7, 2021

NPR’s Jon Hamilton looks back on a decade of Fragile X progress and the Tranfaglia family’s quest for a cure. Hear their story on NPR Short Wave.

COVID-19 Vaccines Pose Little Risk to Rare Disease Patients, FDA, CDC Say

February 2, 2021

COVID-19 vaccines recently approved worldwide are expected to pose little risk to the rare disease community, including Fragile X patients.

Considering Available Drugs for Fragile X: My Favorite Combination (So Far)

February 19, 2020

Which of the available drugs are best for managing fragile X syndrome? Most drugs have “off-target” effects which can have key advantages in some cases.

What Treatments Work for FXTAS?

March 25, 2014

FXTAS affects many in our Fragile X community. Research aims to uncover its cause and guide more effective treatments.

NPR Spotlights Zatolmilast: A Potential Breakthrough for Fragile X Syndrome

NPR Feature – A Fragile X Treatment May Be On The Horizon

COVID-19 Vaccines Pose Little Risk to Rare Disease Patients, FDA, CDC Say

Considering Available Drugs for Fragile X: My Favorite Combination (So Far)

What Treatments Work for FXTAS?

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