Clinical Trials FAQ ← Frequently Asked Questions

Question: How Do Families Decide Which Trial is Best for Them?

Answer: Each of the trials has different requirements for joining, so many – if not most – people will only be eligible for one trial after screening. The best way to approach this is to call the clinic contact closest to your area and discuss this with him/her. Age, weight, current medications, behavior, and IQ are all factors.

When will the Trials be Finished?

It all depends on enrollment. Trials need to have a certain number of people (a number determined before the trial starts) complete the trial before they can analyze the data and present results to the FDA. It all depends on how many people sign up to participate.

Is There Assistance for Travel?

Many trials provide financial assistance for travel expenses. The amount depends on how far you have to travel. Please check with the coordinator at the nearest site to you for more information.

What is an Open Label Extension and Which Trials Offer it?

In these double-blind trials, each participant might be taking either the study drug or placebo (sugar pill). An open label extension means that participants who complete the trial are offered the choice of taking the study drug free of charge for a specified amount of time.

Does My Child Have to be Off of All Medications?

In these double-blind trials, each participant might be taking either the study drug or placebo (sugar pill). An open label extension means that participants who complete the trial are offered the choice of taking the study drug free of charge for a specified amount of time.

How Do I Determine if My Child is Eligible?

You can call the study coordinator at the site at which you would like to participate. They can do a phone screen with you to help determine preliminary eligibility.

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