Forbes, “Clinical Trials Expand For AI-Designed Drug To Treat Fragile X Syndrome”

Forbes, “Clinical Trials Expand For AI-Designed Drug To Treat Fragile X Syndrome”

British startup Healx has secured FDA approval for a phase 2a clinical trial of an AI-discovered compound that could help manage the symptoms of the genetic disorder Fragile X syndrome. The start of the trial marks another milestone in the use of artificial intelligence to help find new applications for existing drugs by mining patient records and research databases.

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The New York Times, “Medical Charities Once Advised on Coping With a Disease. Now They Try to Cure It”

The New York Times, “Medical Charities Once Advised on Coping With a Disease. Now They Try to Cure It”

Propelled by genome sequencing and social media, thousands of charities have sprung up to finance, coordinate and oversee research for cures. Katie Clapp and her son, Andy, who has Fragile X, a disease that causes intellectual disability, with a therapy horse at Gateway Farm in Merrimac, Mass. Ms. Clapp helped form a group that has spent millions on research for a cure.

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Boston Globe, “Playing a part in finding cure for Fragile X”

Boston Globe, “Playing a part in finding cure for Fragile X”

Fragile X is rare and not as highly publicized as many other better-known genetic diseases that attract media interest and generate richer revenue streams of giving. The world of the ailing doesn’t prioritize. There is no Find Help 101 manual for funding charities or what makes the public wake up one day and pour out its heart, empty its wallet, join a bike-a-thon for its cure.

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