Lynne Maquat and Christoph Pröschel standing in a University of Rochester laboratory.

Circular RNA Delivery of FMRP in a Human Neurodevelopmental Model of Fragile X Syndrome

FRAXA-funded researchers explore circular RNA to restore FMRP in Fragile X syndrome, working toward a non-viral treatment that could allow repeat dosing.

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FRAXA Funded Research

Current Research Grants (43)