Many drugs for fragile X syndrome have failed in large clinical trials, but candidates that target new aspects of the condition may fare better.
Read moreSpectrum News – Newly Discovered Aspects of Fragile X Spur Next Wave of Drugs
Bassell, Gary
Gary Bassell, Professor and Chair at Emory University, researches the critical functions of mRNA proteins and their role in neurodegenerative and development disorders.
Genetic and Pharmacologic Manipulation of PI3K Activity in FXS: Assessing Potential Therapeutic Value
With a $90,000 grant from the FRAXA Research Foundation, Dr. Gary Bassell and his team at Emory University explored the PI3K/mTOR signaling complex in FXS via genetic and pharmacologic rescue approaches, to reduce the enzymatic function of specific components of this complex pathway in an FXS mouse model.
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