Characterization and Modulation of microRNAs in Fragile X Syndrome

MicroRNAs are disrupted in Fragile X; the team will work to understand this and explore ways to correct it with drugs which directly target microRNAs.

Read More »
Newly discovered aspects of fragile X spur next wave of drugs

Spectrum News – Newly Discovered Aspects of Fragile X Spur Next Wave of Drugs

Many drugs for Fragile X syndrome have failed in large clinical trials, but candidates that target new aspects of the condition may fare better.

Read More »

Genetic and Pharmacologic Manipulation of PI3K Activity in FXS: Assessing Potential Therapeutic Value

Targeting the PI3K/mTOR cascade — specifically p110β — in Fragile X mice reversed neural and behavioral dysfunctions, validating it as a treatment pathway.

Read More »

Categories

FRAXA Funded Research

Current Research Grants (38)