Maryam Hajfathalian, Michelle James, and colleagues standing outdoors.

Peptide-Functionalized Lipid Nanoparticles for mRNA Delivery to Restore FMRP in Fragile X Syndrome

FRAXA-funded researchers are developing lipid nanoparticles to deliver FMR1 mRNA to brain cells, aiming to restore FMRP in Fragile X syndrome.

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FRAXA Funded Research

Current Research Grants (44)