J. Dora Levin

CRISPR Reactivation of the Fragile X Gene

December 6, 2017

Using CRISPR to reactivate FMRP, “We are trying to target the first event that goes wrong in Fragile X syndrome”, says FRAXA Investigator, Dr. Peter Todd.

Newly Discovered Regulatory Pathways in Fragile X

October 31, 2017

Studies at Yale University and elsewhere show FMRP plays a significant role in regulation of potassium channels. Potassium channel opener drugs could rescue some symptoms of Fragile X.

Healx team David, Dan, Narissa - FRAXA (1)

Drug Repurposing Study Results Accelerate Progress Towards Fragile X Treatments

October 29, 2017

Drug repurposing leverages the detailed information available on approved drugs and reduces the time and money needed to deliver safe “new” treatments, with greater success rates and quicker impact.

Neural Markers of Fragile X: A Powerful New Tool for Clinical Trials

August 17, 2017

Once a neural marker is identified for a particular challenge, it can be measured during drug and behavioral therapy trials to see if a child is improving based on objective biological measures.

CRISPR Reactivation of the Fragile X Gene

Newly Discovered Regulatory Pathways in Fragile X

Drug Repurposing Study Results Accelerate Progress Towards Fragile X Treatments

Neural Markers of Fragile X: A Powerful New Tool for Clinical Trials

Support FRAXA

Get In Touch!

Explore Fragile X & Research

Get FRAXA Updates